Product Candidates

Product Candidates

Pipeline


Hematology

Luspatercept

Hematology

Luspatercept
Preclinical Phase 1 Phase 2 Phase 3
 
Myelodysplastic Syndromes
Myelodysplastic
Syndromes
MEDALIST StudyMEDALIST Study
Long-Term Extension StudyLong-Term Ext St
First-Line Lower-Risk MDS Cohorts1st Line Lower-Risk MDS
Beta-Thalassemia
Beta-Thalassemia
BELIEVE StudyBELIEVE Study
Long-Term Extension StudyLong-Term Ext St
NTD Ph 2 Study (Planned)NTD Ph 2 Planned
Myelofibrosis
Myelofibrosis
Ph 2 Study (Planned)Ph 2 Planned

Preclinical Phase 1 Phase 2 Phase 3
 
Myelofibrosis
Sotatercept
 
Myelofibrosis
Investigator-Sponsored StudyInvest-Sponsored St

Neuromuscular

ACE-083
Preclinical Phase 1 Phase 2 Phase 3
 

Neuromuscular

ACE-083
 
FSH Muscular Dystrophy
FSH Muscular Dystrophy
Part 1 (Ongoing)Pt 1 (Ongoing)
Charcot-Marie-Tooth Disease
Charcot-Marie-Tooth Disease
Ph 2 Study (Planned)Ph 2 Planned