Product Candidates

Product Candidates

Pipeline


Hematology

Luspatercept

Hematology

Luspatercept
PreclinicalPhase 1Phase 2Phase 3
 
Myelodysplastic Syndromes
Myelodysplastic
Syndromes
MEDALIST StudyMEDALIST Study
Long-Term Extension StudyLong-Term Ext St
First-Line Lower-Risk MDS Cohorts1st Line Lower-Risk MDS
Beta-Thalassemia
Beta-Thalassemia
BELIEVE StudyBELIEVE Study
Long-Term Extension StudyLong-Term Ext St
NTD Ph 2 Study (Planned)NTD Ph 2 Planned
Myelofibrosis
Myelofibrosis
Ph 2 Study (Planned)Ph 2 Planned

PreclinicalPhase 1Phase 2Phase 3
 
Myelofibrosis
Sotatercept
 
Myelofibrosis
Investigator-Sponsored StudyInvest-Sponsored St

 

Neuromuscular

ACE-083
PreclinicalPhase 1Phase 2Phase 3

Neuromuscular

ACE-083
FSH Muscular Dystrophy
FSH Muscular Dystrophy
Ph2 Study (Part 1)Ph2
Charcot-Marie-Tooth Disease
Charcot-Marie-Tooth Disease
Ph2 Study (Part 1)Ph 2